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CLINICAL_TRIALS trial_result · 2012-01-05

Clinical Trial Update: Late-Onset Treatment Study Extension Protocol [Phase 4]

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Summary

Phase 4 study extension for late-onset Pompe disease and glycogen storage disease type II; the trial is completed and results were posted in 2012.

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Diseases / indications

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Sponsor: Genzyme, a Sanofi Company | Conditions: Pompe Disease (Late-Onset), Glycogen Storage Disease Type II (GSD-II) | Phase 4 | Status: COMPLETED | Results posted: 2012-01-05