Peroxisome Biogenesis Disorders
📧 Sign up to get email alerts when something new happens for Peroxisome Biogenesis Disorders.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2020-12-17Clinical Trial Update: Hydroxychloroquine Administration for Reduction of Pexophagy [Phase 2]
Phase 2 clinical trial evaluating hydroxychloroquine to reduce pexophagy in Zellweger syndrome and peroxisome biogenesis disorders has compl…
-
CLINICAL_TRIALS trial_result · 2016-06-28Clinical Trial Update: Betaine and Peroxisome Biogenesis Disorders [Phase 3]
Phase 3 trial results evaluated betaine for peroxisome biogenesis disorders; results were posted in 2016.