Peroxisomal Storage Diseases

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CLINICAL_TRIALS trial_result · 2014-07-08
Clinical Trial Update: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases [Phase 3]
Phase 3 trial of ALD-101 as adjuvant therapy with unrelated umbilical cord blood transfusion in inherited metabolic diseases was terminated.