Peroxisomal Disorder
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CLINICAL_TRIALS trial_result · 2016-10-11Clinical Trial Update: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders [NA]
Completed trial evaluating reduced-intensity hematopoietic stem cell transplantation for high-risk lysosomal storage diseases and peroxisoma…