Pelizaeus-merzbacher Disease
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CLINICAL_TRIALS trial_result · 2016-05-13Clinical Trial Update: Long-Term Follow-Up Study of Human Stem Cells Transplanted in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)
This document reports the long-term follow-up of subjects who received human stem cell transplants for Pelizaeus-Merzbacher disease; the tri…
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CLINICAL_TRIALS trial_result · 2015-01-15Clinical Trial Update: Study of Human Central Nervous System (CNS) Stem Cells Transplantation in Pelizaeus-Merzbacher Disease (PMD) Subjects [Phase 1]
This update reports completion of a Phase 1 study evaluating transplantation of human central nervous system stem cells in patients with Pel…