Pearson Syndrome
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CLINICAL_TRIALS trial_result · 2025-11-03Clinical Trial Update: Natural History of Pearson Syndrome
This completed observational clinical trial describes the natural history of Pearson syndrome.
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CLINICAL_TRIALS research · 2025-06-22Clinical Trial Update: Evaluate the Safety and Therapeutic Effects of a Single Intravenous Infusion (IV) of Autologous CD34+ Cells Enriched With Allogenic Placenta-derived Mitochondria in Patients With a Diagnosis of Pearson Syndrome (PS) [Phase 2]
A Phase 2 clinical trial is evaluating the safety and potential therapeutic effects of a single IV infusion of autologous CD34+ cells enrich…
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CLINICAL_TRIALS research · 2025-06-05Clinical Trial Update: Global Registry and Natural History Study for Mitochondrial Disorders
LMU Klinikum is conducting a global registry and natural history study to collect data on mitochondrial disorders, and the study is currentl…
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CLINICAL_TRIALS trial_result · 2021-08-31Clinical Trial Update: A Study to Evaluate the Safety and Therapeutic Effects of Transplantation of MNV-BM-BLD in Pediatric Patients With Pearson Syndrome [Phase 1, Phase 2]
A phase 1/2 clinical trial evaluating safety and therapeutic effects of MNV-BM-BLD transplantation in pediatric patients with Pearson syndro…