Otoferlin-related Nonsyndromic Hearing Loss
📧 Sign up to get email alerts when something new happens for Otoferlin-related Nonsyndromic Hearing Loss.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2024-09-26Clinical Trial Update: A Phase I/II Clinical Trial with SENS-501 in Children Suffering from Severe to Profound Hearing Loss Due to Otoferlin (OTOF) Mutations [Phase 1, Phase 2]
This ClinicalTrials.gov update describes a Phase I/II study of SENS-501 in children with otoferlin-related nonsyndromic hearing loss (DFNB9)…