Non-transfusion-dependent Beta-thalassemia
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CLINICAL_TRIALS trial_result · 2026-03-18Clinical Trial Update: A Study to Test the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the Body [Phase 2]
Phase 2 study to evaluate REGN7999 for iron overload in adults with non-transfusion-dependent beta-thalassemia; the trial is currently recru…
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CLINICAL_TRIALS trial_result · 2025-01-24Clinical Trial Update: A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT) [Phase 3]
ClinicalTrials.gov update for a Phase 3 study evaluating mitapivat in non-transfusion-dependent alpha- or beta-thalassemia; results were pos…