Nijmegen Breakage Syndrome
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CLINICAL_TRIALS research · 2026-01-05Clinical Trial Update: Study of Treosulfan-Based Conditioning for HSCT in Nijmegen Breakage Syndrome [Phase 2]
Phase 2 clinical trial evaluating treosulfan-based conditioning for hematopoietic stem cell transplantation in Nijmegen Breakage Syndrome; c…