Neuronal Ceroid Lipofuscinosis Type
📧 Sign up to get email alerts when something new happens for Neuronal Ceroid Lipofuscinosis Type.
Sign up freeTop drugs studied for this disease
-
FDA approval · 2024-07-10FDA Approved: BRINEURA — Supplemental Application (BioMarin Pharmaceutical Inc.)
FDA approved BioMarin's supplemental application for BRINEURA (cerliponase alfa), updating the approved labeling for the product. This refle…
-
FDA approval · 2018-12-11FDA Approved: BRINEURA — Supplemental Application (BioMarin Pharmaceutical Inc.)
The FDA approved a supplemental application for BRINEURA (cerliponase alfa) from BioMarin Pharmaceutical Inc., updating the drug’s approved …
-
FDA approval · 2017-04-27FDA Approved: BRINEURA — Original Application (BioMarin Pharmaceutical Inc.)
FDA approves Brineura (cerliponase alfa) through the original Biologics License Application by BioMarin for the treatment of neuronal ceroid…