Neuronal Ceroid Lipofuscinoses
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Sign up freeTop drugs studied for this disease
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EMA approval · 2026-06-11EMA Authorised: Brineura (cerliponase alfa) — BioMarin International Limited
EMA confirms authorisation of Brineura (cerliponase alfa) for Neuronal Ceroid-Lipofuscinoses, designated as an orphan medicine with accelera…
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EMA approval · 2023-12-12EMA Authorised: Brineura (cerliponase alfa) — BioMarin International Limited
Brineura (cerliponase alfa) has been authorised by the EMA for Neuronal Ceroid-Lipofuscinoses, with orphan medicine status and accelerated a…