Neurofibromatosis Type
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CLINICAL_TRIALS research · 2025-06-17Clinical Trial Update: Follow-up Study to Evaluate the Safety and Efficacy of FCN-159 in Pediatric Participants With Neurofibromatosis Type 1 [Phase 1, Phase 2]
A registry update describing a Phase 1/Phase 2 follow-up study evaluating FCN-159 in pediatric patients with Neurofibromatosis Type 1, focus…
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CLINICAL_TRIALS research · 2025-06-10Clinical Trial Update: Non-interventional Study of Patients With PN NF1 Starting Selumetinib in Russia
An observational non-interventional study in Russia evaluating outcomes for patients with plexiform neurofibromatosis type 1 starting selume…
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CLINICAL_TRIALS research · 2025-03-06Clinical Trial Update: FCN-159 in Adult Patients With Symptomatic, Inoperable Neurofibromatosis Type 1-Related Plexiform Neurofibromas [Phase 3]
A Phase 3 clinical trial update on FCN-159 for symptomatic, inoperable Neurofibromatosis type 1-related plexiform neurofibromas, sponsored b…
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CLINICAL_TRIALS research · 2025-02-19Clinical Trial Update: Gene Therapy for Neurofibromatosis Type 2 (NF2) with ST002 [NA]
A gene therapy trial for neurofibromatosis type 2 using ST002 is currently NOT_YET_RECRUITING, sponsored by the Cancer Institute and Hospita…
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CLINICAL_TRIALS research · 2024-11-12Clinical Trial Update: Study to Evaluate the Safety, Tolerability, PK Characteristics and Anti-tumor Activity of FCN-159 in Adult and Pediatric Participants With Neurofibromatosis Type 1 [Phase 1, Phase 2]
This Phase 1/2 clinical trial evaluates FCN-159 in adults and children with Neurofibromatosis type 1 and plexiform neurofibroma to assess sa…
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CLINICAL_TRIALS research · 2024-10-09Clinical Trial Update: Antioxidant Therapy With N-acetylcysteine for Children With Neurofibromatosis Type 1 [Phase 2]
A Phase 2 clinical trial evaluating the antioxidant N-acetylcysteine for children with Neurofibromatosis type 1; current status is ACTIVE_NO…
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CLINICAL_TRIALS research · 2024-10-01Clinical Trial Update: Clinical Study on the Treatment of Type I Neurofibromatosis With Smeitinib Hydrosulfate Capsule [Phase 2]
This Clinical Trial Update indicates a Phase 2 study evaluating smeitinib hydrosulfate capsules for Neurofibromatosis type 1, with recruitme…
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CLINICAL_TRIALS research · 2024-09-19Clinical Trial Update: Incidence of Malignant Peripheral Nerve Sheath Tumor (MPNST) Development in Participants With Neurofibromatosis Type 1 (NF1) Receiving and Not Receiving Medical Therapies Directed at Plexiform Neurofibromas (PN)
The NCI-sponsored clinical trial NCT04774289, now completed, compared the incidence of malignant peripheral nerve sheath tumors in people wi…
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CLINICAL_TRIALS research · 2018-07-11Clinical Trial Update: Vision, Attention and Reading in Neurofibromatosis Type 1 (NF1) Children [NA]
This entry reports a clinical study evaluating vision, attention, and reading in children with Neurofibromatosis Type 1, with no phase or st…
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CLINICAL_TRIALS research · 2017-07-25Clinical Trial Update: Neurofibromatosis Type 1 Patient Registry
This entry reports a completed clinical trial registry for Neurofibromatosis Type 1, sponsored by Washington University School of Medicine (…
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CLINICAL_TRIALS research · 2017-05-09Clinical Trial Update: Neurofibromatosis Type 1 Brain Tumor Genetic Risk
Completed clinical trial investigating genetic risk factors for brain tumors in children with Neurofibromatosis Type 1.
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CLINICAL_TRIALS research · 2016-02-11Clinical Trial Update: Analysis of Plasma for Diagnosis and Follow-up of Neurofibromatosis Type 1
This clinical trial update discusses evaluating plasma-based analysis for diagnosing and monitoring neurofibromatosis type 1.
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CLINICAL_TRIALS research · 2014-07-02Clinical Trial Update: Ophthalmological Screening and Follow-up of Optic Pathway Gliomas in Children With Neurofibromatosis Type 1.
The document reports an ongoing clinical trial evaluating ophthalmological screening and follow-up for optic pathway gliomas in children wit…
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CLINICAL_TRIALS research · 2014-06-16Clinical Trial Update: Modifying Genes in Neurofibromatosis 1
This clinical trial update outlines ongoing research on gene modification strategies for Neurofibromatosis type 1.
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CLINICAL_TRIALS research · 2013-01-28Clinical Trial Update: Whole Body Magnetic Resonance Imaging With Diffusion Weighted Imaging : Potential Role in Neurofibromatosis
This clinical trial update discusses using whole-body diffusion-weighted MRI to evaluate neurofibromatosis type 1 and its potential to detec…
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CLINICAL_TRIALS research · 2012-06-25Clinical Trial Update: How Neurofibromatosis Type 1 (NF1) Affects Schoolwork and Self-Esteem
A clinical trial update describing a study on how Neurofibromatosis Type 1 affects schoolwork and self-esteem.
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CLINICAL_TRIALS research · 2011-07-13Clinical Trial Update: First Clinical Study of Erbium - Yttrium Aluminium Garnet (YAG) Laser Vaporization of Cutaneous Neurofibromas [Phase 2, Phase 3]
This document describes the first clinical study using an Erbium-YAG laser to vaporize cutaneous neurofibromas, spanning Phase 2 and Phase 3…
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CLINICAL_TRIALS research · 2010-10-11Clinical Trial Update: Analysis of Peripheral Nerve Sheath Tumors (PNSTs) in Neurofibromatosis Type 1 (NF1) Patients
This entry notes a clinical trial evaluating analysis of peripheral nerve sheath tumors in patients with Neurofibromatosis Type 1, with the …
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CLINICAL_TRIALS research · 2010-10-11Clinical Trial Update: Microarray CGH Analysis of Circulating Tumoral Plasma DNA in NF1 Patients With MPNSTs
A clinical trial update describing a study that analyzes circulating tumoral DNA in Neurofibromatosis Type 1 patients with malignant periphe…