Records containing: Neurofibromatosis 1
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CLINICAL_TRIALS study record update · 2026-04-24A Phase 0/I/II Study of the Cyclin-Dependent Kinase(CDK)4/6 Inhibitor Abemaciclib for Neurofibromatosis Type 1 (NF1) Related Atypical Neurofibromas
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CLINICAL_TRIALS study record update · 2026-04-24A Phase I/II Study of the Mitogen Activated Protein Kinase (MEK) 1 Inhibitor Selumetinib (AZD6244; Hydrogen Sulfate in Children With Neurofibromatosis Type 1 (NF1) and Inoperable Plexiform Neurofibromas (PN)
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CLINICAL_TRIALS study record update · 2026-04-24Development and Validation of Patient Reported Outcome (PRO) Measures for Individuals With Neurofibromatosis 1 (NF1) and Plexiform Neurofibromas (pNFs)
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CLINICAL_TRIALS study record update · 2026-04-22Assessing the Efficacy of Repeat, Monthly Treatments of Cutaneous Neurofibromas (cNFs)
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CLINICAL_TRIALS study record update · 2026-04-15Risk Stratified Treatment for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia: A Phase I/II Non-randomized Study of Trametinib and Azacitidine With or Without Chemotherapy (IND #164058)
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CLINICAL_TRIALS study record update · 2026-04-06Phase II, Open-Label, Prospective Study of T Cell Receptor Alpha/Beta Depletion (A/B TCD) Peripheral Blood Stem Cell (PBSC) Transplantation for Children and Adults With Hematological Malignancies
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CLINICAL_TRIALS study record update · 2026-03-31Real-World Treatment Study of Koselugo (Selumetinib)
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CLINICAL_TRIALS study record update · 2026-03-12Phase 2 Trial of Selumetinib for the Prevention of Plexiform Neurofibroma Growth and Morbidity in Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2026-03-12A Phase 1/1b/2 Study of Cabozantinib in Combination With Selumetinib for Plexiform Neurofibroma in Adults and Adolescents With Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2026-02-27Tailoring an Online Platform to Promote Evidence-Based Care for Adults With Neurofibromatosis 1 and Low Health Literacy
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CLINICAL_TRIALS study record update · 2026-02-19Acceptance and Commitment Therapy for Caregivers of Children With a RASopathy: An Internal Pilot Feasibility Study and Follow-up Phase III Randomized Controlled Trial
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CLINICAL_TRIALS study record update · 2026-02-17A Randomized, Double-Blind, Vehicle-Controlled, Parallel Group Phase 2 Dose-Response Study to Determine Safety and Effectiveness of Two Concentrations of NFX-179 Gel in Subjects With Cutaneous Neurofibromas
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CLINICAL_TRIALS study record update · 2026-01-30A Phase 1 Open Label Study to Assess the Safety, Tolerability, Pharmacokinetics and Clinical Efficacy of Selumetinib, a Selective Mitogen Activated Protein Kinase Kinase (MEK) 1 Inhibitor, in Chinese Paediatric and Adult Subjects With Neurofibromatosis Type 1 (NF1) and Inoperable Plexiform Neurofibromas (PN)
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CLINICAL_TRIALS study record update · 2026-01-13Study of Nutraceutical Intervention With High Phenolic Extra Virgin Olive Oil and Curcumin for Neurofibromatosis, Type 1 (NF1)
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CLINICAL_TRIALS study record update · 2026-01-12Multi-parametric Biomarker Development to Predict Malignant Conversion in Patients With Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2026-01-09Observational Trial of Liquid Biopsy for Malignant Peripheral Nerve Sheath Tumor (MPNST) Among Participants With Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2025-12-24Resiliency Training for Adults With Neurofibromatosis Via Live Videoconferencing
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CLINICAL_TRIALS study record update · 2025-12-18Investigation Into the Natural History and Metabolic and Molecular Basis of RASopathies.
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CLINICAL_TRIALS study record update · 2025-12-02Evaluating Genetic Modifiers of Cutaneous Neurofibromas in Adults With Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2025-11-21Efficacy of Skin Cooling in Reducing Pain Associated With Non-invasive Treatments of Neurofibromatosis Type 1 Cutaneous Neurofibromas
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CLINICAL_TRIALS study record update · 2025-10-20A Phase III, Multicentre, International Study With a Parallel, Randomised, Double-blind, Placebo-controlled, 2 Arm Design to Assess the Efficacy and Safety of Selumetinib in Adult Participants With NF1 Who Have Symptomatic, Inoperable Plexiform Neurofibromas (KOMET)
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CLINICAL_TRIALS study record update · 2025-10-14Natural History Study of Cutaneous Neurofibromas in People With Neurofibromatosis Type 1
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CLINICAL_TRIALS study record update · 2025-10-03A Decentralized Clinical Trial to Promote Evidence-Based Care for Underserved Patients With Neurofibromatosis 1
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CLINICAL_TRIALS study record update · 2025-09-26Surveillance for Malignant Transformation of Neurofibromatosis Type 1 (NF1) Related Peripheral Nerve Sheath Tumors (PNST)
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CLINICAL_TRIALS study record update · 2025-09-02Developing Novel Biomarkers of Plexiform Neurofibroma Tumor Burden