Myotonic Dystrophy

• CLINICAL_TRIALS trial_result · 2026-03-19
  Clinical Trial Update: RAMYD Study - Evaluation of Arrhythmic Risk in Myotonic Dystrophy [NA]

  RAMYD Study completed evaluating arrhythmic risk in patients with Myotonic Dystrophy.

• CLINICAL_TRIALS trial_result · 2024-11-25
  Clinical Trial Update: Open Label Study in Adolescents and Children With Myotonic Disorders [Phase 3]

  Open-label Phase 3 study in children and adolescents with myotonic dystrophy has completed, sponsored by Lupin Ltd.

• CLINICAL_TRIALS trial_result · 2024-09-19
  Clinical Trial Update: The Risk of Falls Index for Patients With Neuromuscular Disorders

  A completed trial evaluating a Falls Index to assess fall risk in patients with neuromuscular disorders, including Inclusion Body Myositis, …

• CLINICAL_TRIALS trial_result · 2021-06-23
  Clinical Trial Update: Safety, Tolerability and Pharmacokinetics of ERX-963 in Adults With Myotonic Dystrophy Type 1 [Phase 1]

  Phase 1 study assessing safety, tolerability, and pharmacokinetics of ERX-963 in adults with myotonic dystrophy type 1 has been completed wi…

• CLINICAL_TRIALS trial_result · 2017-03-10
  Clinical Trial Update: Efficacy and Tolerance of AVAPS Mode in Myotonic Dystrophy [NA]

  A completed clinical trial evaluated the efficacy and tolerance of AVAPS ventilation mode in patients with myotonic dystrophy.

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• CLINICAL_TRIALS trial_result · 2013-01-28
  Clinical Trial Update: Study of Muscle Wasting and Altered Metabolism in Patients With Myotonic Dystrophy

  This entry notes the completion of a clinical trial studying muscle wasting and altered metabolism in patients with myotonic dystrophy.

• CLINICAL_TRIALS trial_result · 2010-11-16
  Clinical Trial Update: Postural Spirometry Changes in Ambulatory Myotonic Dystrophy Patients [NA]

  An update from the University of Nancy describes postural spirometry changes observed in ambulatory patients with myotonic dystrophy. The st…

• CLINICAL_TRIALS trial_result · 2010-04-06
  Clinical Trial Update: Efficacy and Safety of DHEA for Myotonic Dystrophy [Phase 2, Phase 3]

  An update on phase 2/3 trials evaluating the efficacy and safety of dehydroepiandrosterone (DHEA) for myotonic dystrophy.