Mucopolysaccharidosis Type Vii
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CLINICAL_TRIALS trial_result · 2018-02-19Clinical Trial Update: A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7) [Phase 3]
Phase 3 study of UX003 rhGUS enzyme replacement therapy for MPS type 7 (Sly syndrome) completed with results posted in 2018.