Mucopolysaccharidosis Type Vi
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CLINICAL_TRIALS trial_result · 2024-11-22Clinical Trial Update: Gene Therapy in Patients With Mucopolysaccharidosis Disease [Phase 1, Phase 2]
This clinical trial update reports completion of a Phase 1/2 gene therapy study in patients with Mucopolysaccharidosis Type VI. The status o…
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CLINICAL_TRIALS trial_result · 2024-10-22Clinical Trial Update: Longitudinal Study of Bone Disease in Children with Mucopolysaccharidoses (MPS) I, II, and VI
This clinical trial update reports on a longitudinal study of bone disease in children with mucopolysaccharidoses types I, II, and VI. The s…
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CLINICAL_TRIALS trial_result · 2017-09-15Clinical Trial Update: Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI [Phase 1, Phase 2]
Clinical trial evaluating adalimumab in mucopolysaccharidosis types I, II, and VI has completed phases 1 and 2 with results posted in 2017.
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CLINICAL_TRIALS trial_result · 2014-04-02Clinical Trial Update: Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02
This is a completed observational study of patients with Mucopolysaccharidosis type VI who previously participated in ASB-00-02, sponsored b…
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CLINICAL_TRIALS trial_result · 2010-10-15Clinical Trial Update: A Phase 4 Two Dose Level Study of Naglazyme(TM) (Galsulfase) in Infants With MPS VI [Phase 4]
This clinical trial update reports Phase 4 results from a two-dose level study of Naglazyme (galsulfase) in infants with Mucopolysaccharidos…
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CLINICAL_TRIALS trial_result · 2009-08-25Clinical Trial Update: Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI [Phase 2]
Open-label Phase 2 study evaluating the efficacy and safety of Naglazyme (recombinant human N-acetylgalactosamine 4-sulfatase) in patients w…
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CLINICAL_TRIALS trial_result · 2009-08-17Clinical Trial Update: Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients With MPS VI [Phase 3]
A Phase 3 trial of recombinant human N-acetylgalactosamine 4-sulfatase (galsulfase) for mucopolysaccharidosis type VI has completed and resu…