Mucopolysaccharidosis Type Iii Sanfilippo
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CLINICAL_TRIALS trial_result · 2018-04-17Clinical Trial Update: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously [Phase 1, Phase 2]
Open-label Phase 1/2 trial of SBC-103 in MPS IIIB patients to evaluate safety, pharmacokinetics, and pharmacodynamics/efficacy; the study wa…