Mucopolysaccharidosis Iiib

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CLINICAL_TRIALS trial_result · 2018-07-12
Clinical Trial Update: Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Type B (MPS IIIB) [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating SBC-103 for Mucopolysaccharidosis IIIB has completed, with results posted in 2018.