Records containing: Mucopolysaccharidosis

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CLINICAL_TRIALS study record update · 2021-08-16
Effects of Enzyme Replacement Therapy on Quality of Life, Functional Independence and Aerobic Capacity in Children With Mucopolysaccharidosis
CLINICAL_TRIALS study record update · 2019-10-16
An Open-label Study of UX003 rhGUS Enzyme Replacement Therapy in MPS 7 Patients Less Than 5 Years Old
CLINICAL_TRIALS study record update · 2019-07-30
A Long-Term Open-Label Treatment and Extension Study of UX003 rhGUS Enzyme Replacement Therapy in Subjects With MPS 7
CLINICAL_TRIALS study record update · 2018-02-19
A Randomized, Placebo-Controlled, Blind-Start, Single-Crossover Phase 3 Study to Assess the Efficacy and Safety of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7
CLINICAL_TRIALS study record update · 2017-05-12
Allogeneic Hematopoietic Stem Cell Transplantation for Standard Risk Inherited Metabolic Disorders
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CLINICAL_TRIALS study record update · 2014-07-08
A Phase III Trial of ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transplantation (UCBT) in Patients With Inborn Errors of Metabolism
CLINICAL_TRIALS study record update · 2013-03-01
Corneal-Compensated Intraocular Pressure, Corneal Hysteresis and Corneal Resistance Factor Measurements Performed With the Ocular Response Analyzer and Their Correlation to Conventional Goldmann Applanation Tonometry.
CLINICAL_TRIALS study record update · 2012-06-04
Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis