Mucolipidosis Type Iv
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CLINICAL_TRIALS research · 2026-04-23Clinical Trial Update: Mucolipidosis Type IV Natural History Study
Update on a natural history study of Mucolipidosis Type IV showing the study is currently active but not recruiting.
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CLINICAL_TRIALS research · 2026-02-10Clinical Trial Update: Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV [Phase 1]
This Clinical Trial Update covers a Phase 1 study of AAV9.hMCOLN1co for patients with Mucolipidosis Type IV. The study is currently enrollin…
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CLINICAL_TRIALS research · 2017-07-02Clinical Trial Update: The Natural History and Pathogenesis of Mucolipidosis Type IV
This clinical trial update summarizes the natural history and pathogenesis of Mucolipidosis Type IV based on completed study NCT00015782.