Molybdenum Cofactor Deficiency Type
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CLINICAL_TRIALS trial_result · 2023-10-17Clinical Trial Update: Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A [Phase 2, Phase 3]
A Phase 2/3 study evaluating ORGN001 (formerly ALXN1101) in neonates, infants, and children with Molybdenum Cofactor Deficiency Type A has c…
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CLINICAL_TRIALS trial_result · 2023-10-17Clinical Trial Update: Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treated With rcPMP [Phase 2]
Phase 2 clinical trial update on ORGN001 (formerly ALXN1101) in pediatric MoCD Type A patients on rcPMP, completed with results posted in 20…