Methylmalonic Acidemia
📧 Sign up to get email alerts when something new happens for Methylmalonic Acidemia.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS withdrawal · 2024-09-24Clinical Trial Update: A Study to Evaluate the Safety, Tolerability, and Pharmacodynamics of SEL-302 in Pediatric Subjects With MMA [Phase 1, Phase 2]
The clinical trial NCT05778877 evaluating SEL-302 in pediatric patients with methylmalonic acidemia has been withdrawn, with no further enro…
-
CLINICAL_TRIALS withdrawal · 2014-05-29Clinical Trial Update: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate [Phase 2]
Phase 2 trial of N-Carbamylglutamate to increase ureagenesis in urea cycle disorders and other inborn errors of metabolism has been withdraw…