Methylmalonic Acidemia with Homocystinuria Cblc Type
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CLINICAL_TRIALS trial_result · 2017-04-25Clinical Trial Update: EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment [Phase 2]
Phase 2 trial of EPI-743 in cblC-type methylmalonic acidemia with homocystinuria evaluated effects on visual and neurologic impairment; the …