Metabolism Inborn Errors

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EMA approval · 2026-08-24
EMA Authorised: Chenodeoxycholic acid Leadiant (previously Chenodeoxycholic acid sigma-tau) (chenodeoxycholic acid) — Leadiant Biosciences Ireland Limited
The EMA authorises chenodeoxycholic acid (Leadiant) for Xanthomatosis, Cerebrotendinous and Metabolism, Inborn Errors; designated as an orph…