Lipin-1 Deficiency
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CLINICAL_TRIALS withdrawal · 2026-03-27Clinical Trial Update: International Multicenter Study on Lipin-1 Deficiency
An international multicenter clinical trial update for Lipin-1 Deficiency reports that the study has been terminated.
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CLINICAL_TRIALS withdrawal · 2025-09-25Clinical Trial Update: Acute Rhabdomyolysis and Muscle Pain Associated With Mutations in the LPIN1 Gene - A Retrospective Study Describing the Safety and Efficacy of Hydroxychloroquine Sulfate Given on a Compassionate Basis to Patients Suffering From Lipin-1 Deficiency
A retrospective study evaluated compassionate-use hydroxychloroquine sulfate in patients with Lipin-1 deficiency, focusing on safety and rha…