Limb-girdle Muscular Dystrophy Type
📧 Sign up to get email alerts when something new happens for Limb-girdle Muscular Dystrophy Type.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-03-02Clinical Trial Update: A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4 [Phase 3]
Sarepta Therapeutics reports a Phase 3 trial of Bidridistrogene Xeboparvovec (SRP-9003) for limb-girdle muscular dystrophy type 2E/R4; the s…
-
CLINICAL_TRIALS trial_result · 2025-10-06Clinical Trial Update: ATA-100 (Formerly GNT0006) Gene Therapy Trial in Patients With LGMDR9 [Phase 1]
Update on Atamyo Therapeutics' ATA-100 gene therapy trial for limb-girdle muscular dystrophy type 9 (LGMDR9), currently in Phase 1 and liste…