Limb-girdle Muscular Dystrophy Type 2e
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CLINICAL_TRIALS trial_result · 2026-02-19Clinical Trial Update: A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency) [Phase 1]
Phase 1 gene transfer trial SRP-9003 for limb-girdle muscular dystrophy type 2E/beta-sarcoglycan deficiency is active but not recruiting, ev…
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CLINICAL_TRIALS trial_result · 2026-01-20Clinical Trial Update: Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency) [Phase 1, Phase 2]
The trial update for Sarepta's SRP-9003 gene therapy for limb-girdle muscular dystrophy type 2E shows the Phase 1/2 study has been terminate…
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CLINICAL_TRIALS trial_result · 2025-08-14Clinical Trial Update: Natural History of Limb Girdle Muscular Dystrophy Type 2A and Type 2E
This clinical trial update indicates that the natural history study of limb-girdle muscular dystrophy type 2A and type 2E has completed.