Limb-girdle Muscular Dystrophy Type 2b
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CLINICAL_TRIALS research · 2025-11-18Clinical Trial Update: Long-Term Development of Muscular Dystrophy Outcome Assessments
Clinical trial update indicating ongoing recruitment for a long-term study assessing outcome measures in limb-girdle muscular dystrophy acro…
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CLINICAL_TRIALS trial_result · 2025-09-04Clinical Trial Update: A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2B/R2 (LGMD2B/R2, Dysferlin [DYSF] Related) [Phase 1]
Sarepta's Phase 1 gene transfer study SRP-6004 in ambulatory participants with limb-girdle muscular dystrophy type 2B (DYSF-related) has bee…
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CLINICAL_TRIALS research · 2025-06-27Clinical Trial Update: Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF
A clinical trial in the Russian Federation is enrolling by invitation to study the immunological, morphological, and genetic characteristics…
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CLINICAL_TRIALS trial_result · 2024-07-18Clinical Trial Update: Dysferlinopathy Protein in Peripheral Blood Monocytes.
A completed clinical trial investigating the dysferlinopathy protein in peripheral blood monocytes in muscular dystrophy conditions, includi…
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CLINICAL_TRIALS trial_result · 2023-10-19Clinical Trial Update: Evaluate Safety and Biological Activity of ATYR1940 in Participants With Limb Girdle Muscular Dystrophy 2B (LGMD2B) and Facioscapulohumeral Muscular Dystrophy (FSHD) [Phase 1, Phase 2]
Phase 1/2 trial evaluating ATYR1940 for safety and biological activity in LGMD2B and FSHD has completed with results posted.
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CLINICAL_TRIALS trial_result · 2015-09-02Clinical Trial Update: Deflazacort in Dysferlinopathies [Phase 2, Phase 3]
Phase 2 and Phase 3 clinical trials evaluating deflazacort for dysferlinopathies (Limb-girdle muscular dystrophy type 2B and Miyoshi myopath…
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CLINICAL_TRIALS trial_result · 2014-03-07Clinical Trial Update: Evaluation of Limb-Girdle Muscular Dystrophy
A completed clinical trial update evaluating therapies for several limb-girdle muscular dystrophy subtypes, including LGMD type 2A, 2B, and …