Records containing: Leber Congenital Amaurosis (LCA)
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CLINICAL_TRIALS study record update · 2025-06-18Psychotherapy Group for Parents of Children With Leber Congenital Amaurosis
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CLINICAL_TRIALS study record update · 2024-04-11Long-term Follow-up Study of Participants Following an Open Label, Multi-centre, Phase I/II Dose Escalation Trial of an Adeno-associated Virus Vector (AAV2/5-OPTIRPE65) for Gene Therapy of Adults and Children With Retinal Dystrophy Owing to Defects in RPE65 (LCA2)
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CLINICAL_TRIALS study record update · 2016-04-29Retrospective, Uncontrolled, Multicenter, Case History Study to Determine the Natural History of Visual Function in Subjects With Inherited Retinal Disease (IRD) Caused by Inherited Mutation of Retinal Pigment Epithelial 65 Protein (RPE65) or Lecithin:Retinol Acyltransferase (LRAT)