Infantile Metachromatic Leukodystrophy
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CLINICAL_TRIALS trial_result · 2013-11-08Clinical Trial Update: Open-Label Extension Study of Recombinant Human Arylsulfatase A (HGT-1111) in Late Infantile MLD [Phase 2]
Phase 2 open-label extension trial for recombinant human arylsulfatase A (HGT-1111) in late infantile metachromatic leukodystrophy has termi…
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CLINICAL_TRIALS trial_result · 2012-06-15Clinical Trial Update: Long-term Metazym Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) [Phase 1, Phase 2]
A long-term study of Metazym in patients with late infantile metachromatic leukodystrophy completed with results posted in 2012.