Records containing: Inherited Retinal Dystrophy Associated With RPE65 Mutations
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CLINICAL_TRIALS study record update · 2026-03-06A Multi-center Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of rAAV2-RPE65 Gene Therapy (LX101) in Subjects With Biallelic RPE65 Mutation-associated Inherited Retinal Dystrophy
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CLINICAL_TRIALS study record update · 2026-03-05Efficacy and Safety of Gene Therapy rAAV-RPE65 (LX101) in Biallelic RPE65 Mutation-associated Inherited Retinal Dystrophy: a Phase III, Multicenter, Randomized Controlled Trial (STAR)