Inherited Retinal Diseases Caused By Rpe65 Mutations

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CLINICAL_TRIALS research · 2024-09-19
Clinical Trial Update: Safety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR) [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating HG004 for Leber congenital amaurosis due to RPE65 mutations is currently recruiting.