Inherited Metabolic Disorders
📧 Sign up to get email alerts when something new happens for Inherited Metabolic Disorders.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2024-07-12Clinical Trial Update: Haploidentical Allogeneic Hematopoietic Stem Cell Transplantation (HaploHCT) Following Reduced Intensity Conditioning (RIC) for Selected High Risk Non-Malignant Diseases [Phase 2]
This Phase 2 clinical trial update reports the termination of a haploidentical hematopoietic stem cell transplantation study using reduced-i…
-
CLINICAL_TRIALS trial_result · 2021-10-28Clinical Trial Update: MGTA-456 in Patients With Inherited Metabolic Disorders Undergoing Hematopoietic Stem Cell Transplantation (HSCT) [Phase 2]
Phase 2 clinical trial update for MGTA-456 in patients with inherited metabolic disorders undergoing HSCT; study completed with results post…
-
CLINICAL_TRIALS trial_result · 2018-10-10Clinical Trial Update: A Trial of a Single ProHema-CB Product Transplant in Pediatric Patients With Inherited Metabolic Disorders [Phase 1]
Phase 1 clinical trial in pediatric patients with inherited metabolic disorders using a single ProHema-CB product transplant was terminated;…