Infantile-onset Pompe Disease
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CLINICAL_TRIALS approval · 2014-02-05Clinical Trial Update: Expanded Access Use of Myozyme (Alglucosidase Alfa) in Patients With Infantile-onset Pompe Disease
This update covers expanded access use of Myozyme (alglucosidase alfa) for infantile-onset Pompe disease and notes marketing approval for th…