Inborn Errors of Metabolism
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CLINICAL_TRIALS withdrawal · 2017-06-29Clinical Trial Update: Fetal Umbilical Cord Blood (UCB) Transplant for Lysosomal Storage Diseases [Phase 1]
Phase 1 fetal umbilical cord blood transplant trial for lysosomal storage diseases has been withdrawn.
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CLINICAL_TRIALS withdrawal · 2014-05-29Clinical Trial Update: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate [Phase 2]
Phase 2 trial of N-Carbamylglutamate to increase ureagenesis in urea cycle disorders and other inborn errors of metabolism has been withdraw…