Hyper-igm Syndrome
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: Base Editing Hematopoietic Stem Cell and T Cell Gene Therapy for CD40L-HyperIgM Syndrome: Single Patient Study [Phase 1, Phase 2]
A single-patient, phase 1/2 clinical trial is exploring base editing of hematopoietic stem cells and T cells to treat CD40L-HyperIgM Syndrom…