Hutchinson-gilford Progeria Syndrome
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EMA approval · 2026-04-07EMA Authorised: Zokinvy (Lonafarnib) — TMC Pharma (EU) Limited
The European Medicines Agency authorised Zokinvy (lonafarnib) for Hutchinson-Gilford progeria syndrome and laminopathies in the European Uni…
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CLINICAL_TRIALS trial_result · 2026-02-09Clinical Trial Update: Study to Determine Optimal Dose and Evaluate Safety, Tolerability, and Pharmacokinetics of Progerinin in Patients With Hutchinson-Gilford Progeria Syndrome (HGPS) [Phase 2]
A Phase 2 clinical trial update for Progerinin in Hutchinson-Gilford Progeria Syndrome to determine optimal dosing and assess safety, tolera…
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FDA approval · 2024-03-21FDA Approved: ZOKINVY — Supplemental Application (Sentynl Therapeutics, Inc.)
FDA approved a supplemental application for ZOKINVY (lonafarnib) from Sentynl Therapeutics, Inc. under NDA 213969. The action approves chang…
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EMA approval · 2022-05-20First treatment for children with Progeria or progeroid like syndromes (rare premature aging syndromes)
EMA announces first treatment for children with Progeria and other progeroid syndromes, offering a targeted option for these rare premature …
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FDA approval · 2020-11-20FDA Approved: ZOKINVY — Original Application (Sentynl Therapeutics, Inc.)
The FDA approved Zokinvy (lonafarnib) from Sentynl Therapeutics for Hutchinson-Gilford Progeria Syndrome and processing-deficient progeroid …
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CLINICAL_TRIALS trial_result · 2020-11-04Clinical Trial Update: Umbilical Cord Blood Transfusion in Progeria Syndrome [Phase 1, Phase 2]
Phase 1/2 clinical trial on umbilical cord blood transfusion for Hutchinson-Gilford Progeria Syndrome has completed.
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CLINICAL_TRIALS trial_result · 2017-05-24Clinical Trial Update: Phase II Trial of Lonafarnib (a Farnesyltransferase Inhibitor) for Progeria [Phase 2]
Phase II trial of lonafarnib for Progeria (Hutchinson-Gilford Progeria syndrome) completed; results posted.
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CLINICAL_TRIALS trial_result · 2013-07-08Clinical Trial Update: Treatment of the Hutchinson-Gilford Progeria Syndrome With a Combination of Pravastatin and Zoledronic Acid [Phase 2]
A Phase 2 clinical trial evaluating a combination of pravastatin and zoledronic acid for Hutchinson-Gilford Progeria Syndrome has completed,…