Homocystinuria
📧 Sign up to get email alerts when something new happens for Homocystinuria.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-02-19Clinical Trial Update: Evaluation of the Express Plus Range [NA]
A completed clinical trial evaluated Vitaflo's Express Plus Range for multiple metabolic disorders including phenylketonuria, homocystinuria…
-
CLINICAL_TRIALS trial_result · 2025-04-11Clinical Trial Update: A Phase 3 Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE) [Phase 3]
This Phase 3 long-term extension study, ENSEMBLE, aims to assess the long-term safety and efficacy of pegTibatinase in participants aged 5 t…
-
CLINICAL_TRIALS trial_result · 2023-02-03Clinical Trial Update: Betaine METABOLISM OF PATIENTS With Homocystinuria [Phase 2]
Phase 2 clinical trial update on betaine metabolism in patients with homocystinuria; study status completed.
-
CLINICAL_TRIALS trial_result · 2018-07-09Clinical Trial Update: Oxidative Stress Markers In Inherited Homocystinuria And The Impact Of Taurine [Phase 1, Phase 2]
Phase 1/2 trial evaluating oxidative stress markers in inherited homocystinuria and the impact of taurine; results were posted in 2018.
-
CLINICAL_TRIALS trial_result · 2017-10-16Clinical Trial Update: Vitamin D3 Treatment and Homocysteine Concentrations Among Overweight Reproductive Women [Phase 2]
Phase 2 trial evaluating Vitamin D3 (cholecalciferol) treatment and its effect on homocysteine levels in overweight reproductive-age women; …
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS trial_result · 2009-02-18Clinical Trial Update: Homocystinuria: Treatment With N-Acetylcysteine [Phase 2]
A Phase 2 clinical trial evaluating N-Acetylcysteine for treatment of homocystinuria has completed.