Hereditary Transthyretin-mediated Amyloid Polyneuropathy
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CLINICAL_TRIALS research · 2025-12-04Clinical Trial Update: A Study to Assess the Long-Term Safety and Efficacy of Eplontersen (Formerly Known as ION-682884, IONIS-TTR-LRx and AKCEA-TTR-LRx) in Patients With Hereditary Transthyretin-Mediated Amyloid Polyneuropathy [Phase 3]
A Phase 3 long-term safety and efficacy trial of Eplontersen for hereditary transthyretin-mediated amyloid polyneuropathy is ongoing and cur…