Hereditary Transthyretin Amyloidosis with Polyneuropathy
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CLINICAL_TRIALS trial_result · 2026-01-30Clinical Trial Update: Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (ATTRv-PN) and Patients With Transthyretin Amyloidosis-Related Cardiomyopathy (ATTR-CM) [Phase 1]
Phase 1 study of NTLA-2001 in hereditary transthyretin amyloidosis with polyneuropathy and transthyretin amyloid cardiomyopathy has complete…
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CLINICAL_TRIALS trial_result · 2025-04-10Clinical Trial Update: A Study to Characterize Adverse Events Occurring Within One Day of TEGSEDI Administration to Adult Participants With hATTR-PN [Phase 4]
Phase 4 study evaluating adverse events within one day of TEGSEDI administration in adults with hereditary transthyretin amyloidosis with po…