Hereditary Transthyretin Amyloidosis
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Southeastern ATTR Amyloidosis Consortium: SEATTRAC Family Registry
This entry describes the SEATTRAC Family Registry, a clinical trial registry for hereditary transthyretin amyloidosis, sponsored by Virginia…
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CLINICAL_TRIALS trial_result · 2026-04-07Clinical Trial Update: Hereditary Transthyretin Amyloidosis Polyneuropathy in Patients With Carpal Tunnel Syndrome in Russia
This document reports the completion of a clinical trial investigating hereditary transthyretin amyloidosis with polyneuropathy in patients …
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CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: Comprehensive Program for Hereditary Transthyretin Amyloidosis
Clinical trial update announcing a comprehensive program for hereditary transthyretin amyloidosis that is currently recruiting.
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CLINICAL_TRIALS trial_result · 2026-03-12Clinical Trial Update: Monitoring of Early Disease Progression in Hereditary Transthyretin Amyloidosis
Completed clinical trial update describing approaches to monitoring early disease progression in hereditary transthyretin amyloidosis. The s…
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CLINICAL_TRIALS research · 2026-01-02Clinical Trial Update: ATTR Amyloid Cardiomyopathy: Characterization of Extracellular Vesicles as Potential Disease Stratifiers and Prognostic Biomarkers
This clinical trial update describes a study on extracellular vesicles as potential disease stratifiers and prognostic biomarkers for transt…
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CLINICAL_TRIALS research · 2025-06-24Clinical Trial Update: Exercise in Hereditary ATTR (ATTRv) Amyloidosis [NA]
A clinical trial update indicates a study evaluating exercise in patients with hereditary transthyretin amyloidosis (ATTRv) is currently rec…
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CLINICAL_TRIALS trial_result · 2025-05-25Clinical Trial Update: hATTR Polyneuropathy in Russia
AstraZeneca-sponsored clinical trial evaluating hereditary transthyretin amyloidosis with polyneuropathy in Russia has completed.
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CLINICAL_TRIALS trial_result · 2024-11-22Clinical Trial Update: Transthyretin Amyloidosis Outcome Survey (THAOS)
Pfizer-sponsored THAOS transthyretin amyloidosis registry study has completed and posted results.
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CLINICAL_TRIALS trial_result · 2024-09-24Clinical Trial Update: Exploring Biomarkers in Hereditary Transthyretin Amyloidosis [NA]
A study investigating biomarkers in hereditary transthyretin amyloidosis is currently recruiting.
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: A Study to Examine the Clinical Effectiveness of Tafamidis in Patients With Mixed Phenotype Hereditary Transthyretin Amyloidosis
Pfizer completed a trial evaluating Tafamidis in mixed-phenotype hereditary transthyretin amyloidosis with cardiomyopathy. Results from the …
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CLINICAL_TRIALS trial_result · 2024-05-13Clinical Trial Update: Retrospective Study Collecting Neurological Follow-up of Hereditary Transthyretin Amyloidosis (ATTRv) Patients Included in B3461028 and B3461045.
This is a completed retrospective study collecting neurological follow-up data from hereditary transthyretin amyloidosis (ATTRv) patients en…
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CLINICAL_TRIALS trial_result · 2022-08-11Clinical Trial Update: HELIOS-A: A Study of Vutrisiran (ALN-TTRSC02) in Patients With Hereditary Transthyretin Amyloidosis (hATTR Amyloidosis) [Phase 3]
HELIOS-A, a Phase 3 study of vutrisiran (ALN-TTRSC02) in patients with hereditary transthyretin amyloidosis (hATTR) has completed and posted…
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CLINICAL_TRIALS trial_result · 2018-07-18Clinical Trial Update: ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) [Phase 3]
Phase 3 ENDEAVOUR trial evaluating Revusiran (ALN-TTRSC) in transthyretin-mediated familial amyloid cardiomyopathy has completed with result…