Hereditary Neuropathy Caused By Sorbitol Dehydrogenase Deficiency
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CLINICAL_TRIALS trial_result · 2025-09-15Clinical Trial Update: Pharmacodynamic EffIcacy and Clinical Benefit of AT 007 in Patients With Sorbitol Dehydrogenase (SORD) Deficiency [Phase 2, Phase 3]
Phase 2/Phase 3 clinical trial update evaluating AT 007 in patients with hereditary neuropathy caused by sorbitol dehydrogenase (SORD) defic…