Hereditary Angioedema
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CLINICAL_TRIALS trial_result · 2025-12-23Clinical Trial Update: Open-label Berotralstat Access to HAE Patients Previously Enrolled in Berotralstat Studies [Phase 3]
Open-label access for Berotralstat is being offered to hereditary angioedema patients who were previously enrolled in Berotralstat studies, …
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CLINICAL_TRIALS trial_result · 2025-12-18Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of Icatibant in Patients With Bradykinin Induced Angioedema [Phase 4]
A Phase 4 clinical trial evaluating the safety and efficacy of icatibant in patients with bradykinin-mediated angioedema and hereditary angi…
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CLINICAL_TRIALS trial_result · 2025-12-17Clinical Trial Update: Dose-ranging Study of Oral PHA-022121 for Acute Treatment of Angioedema Attacks in Patients With Hereditary Angioedema [Phase 2]
Phase 2 dose-ranging study evaluating oral PHA-022121 for acute treatment of angioedema attacks in patients with hereditary angioedema. The …
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CLINICAL_TRIALS trial_result · 2025-11-28Clinical Trial Update: Long-Term Follow-Up (LTFU) of Subjects Treated With NTLA 2002
This update reports long-term follow-up data for subjects treated with NTLA-2002 in hereditary angioedema, with ongoing enrollment by invita…
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CLINICAL_TRIALS trial_result · 2025-11-21Clinical Trial Update: Study of Oral Deucrictibant Soft Capsule for On-Demand Treatment of Angioedema Attacks in Adolescents and Adults With Hereditary Angioedema [Phase 3]
Phase 3 study of oral deucrictibant for on-demand treatment of hereditary angioedema attacks in adolescents and adults has completed.
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CLINICAL_TRIALS trial_result · 2025-11-17Clinical Trial Update: 12-Week Safety and Efficacy Study of BCX4161 as an Oral Prophylaxis Against HAE Attacks [Phase 2, Phase 3]
BioCryst reports results from a 12-week safety and efficacy study of BCX4161 as an oral prophylaxis for hereditary angioedema (HAE) in a com…
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CLINICAL_TRIALS trial_result · 2025-09-08Clinical Trial Update: Post Study Access of CSL312 (Garadacimab) for Pediatric Participants With Hereditary Angioedema Who Have Completed the CSL312_3003 Study
Post-study access for pediatric participants who completed the CSL312_3003 trial evaluating garadacimab (CSL312) for hereditary angioedema.
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CLINICAL_TRIALS trial_result · 2025-09-02Clinical Trial Update: A Study of Lanadelumab in Persons With Hereditary Angioedema (HAE) Type I or II
This document reports an update from a completed clinical trial evaluating lanadelumab in individuals with hereditary angioedema type I or I…
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CLINICAL_TRIALS trial_result · 2025-07-30Clinical Trial Update: Dose-ranging Study of Oral PHA-022121 for Prophylaxis Against Angioedema Attacks in Patients With Hereditary Angioedema Type I or Type II [Phase 2]
A Phase 2 dose-ranging study of oral PHA-022121 for prophylaxis against angioedema attacks in patients with hereditary angioedema (Types I a…
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CLINICAL_TRIALS trial_result · 2025-07-11Clinical Trial Update: Donidalorsen Expanded Access Program for Patients With Hereditary Angioedema
This update confirms an expanded access program for donidalorsen in patients with hereditary angioedema, allowing eligible patients to acces…
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CLINICAL_TRIALS trial_result · 2025-04-29Clinical Trial Update: A Single Dose Safety, Tolerability, Pharmacokinetic and Food Effect Study of KVD900 (Sebetralstat) in Healthy Volunteers [Phase 1]
Phase 1 study evaluating the safety, tolerability, pharmacokinetics and food effect of a single dose of KVD900 (Sebetralstat) in healthy vol…
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CLINICAL_TRIALS trial_result · 2025-04-11Clinical Trial Update: A Study of STAR-0215 in Participants With Hereditary Angioedema [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating STAR-0215 in participants with hereditary angioedema has been completed.
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CLINICAL_TRIALS trial_result · 2025-03-24Clinical Trial Update: An Extension Study of Donidalorsen (IONIS-PKK-LRx) in Participants With Hereditary Angioedema [Phase 2]
Phase 2 extension study of Donidalorsen (IONIS-PKK-LRx) in participants with hereditary angioedema has completed.
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CLINICAL_TRIALS trial_result · 2025-03-06Clinical Trial Update: OASIS-HAE: A Study to Evaluate the Safety and Efficacy of Donidalorsen (ISIS 721744 or IONIS-PKK-LRx) in Participants With Hereditary Angioedema (HAE) [Phase 3]
Phase 3 trial results update for donidalorsen in hereditary angioedema (HAE) from the OASIS-HAE study, with results posted in March 2025.
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: FIRAZYR General Drug Use-Results Survey (Japan)
A completed Japan-based survey evaluating real-world use of Firazyr (icatibant) for hereditary angioedema, with results posted in 2025.
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CLINICAL_TRIALS trial_result · 2025-02-10Clinical Trial Update: A Study to Explore Hereditary Angioedema (HAE) Symptoms and Treatment Patterns in Korean People
This completed clinical study conducted in Korean participants investigated hereditary angioedema symptoms and treatment patterns.
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CLINICAL_TRIALS trial_result · 2024-12-13Clinical Trial Update: A Study of Lanadelumab (SHP643) in Chinese Participants With Hereditary Angioedema (HAE) [Phase 3]
Phase 3 study of Lanadelumab (SHP643) in Chinese participants with hereditary angioedema has completed and results have been posted.
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CLINICAL_TRIALS trial_result · 2024-11-15Clinical Trial Update: Treatment of Hereditary Angioedema Prodrome with Recombinant C1-esterase Inhibitor (Ruconest) [Phase 4]
A Phase 4 trial evaluating the treatment of hereditary angioedema prodrome with recombinant C1-esterase inhibitor (Ruconest) has completed.
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CLINICAL_TRIALS trial_result · 2024-10-28Clinical Trial Update: Firazyr® Patient Registry (Icatibant Outcome Survey - IOS)
This document reports the completed status of the Firazyr patient registry, the Icatibant Outcome Survey (IOS), tracking outcomes in heredit…
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CLINICAL_TRIALS trial_result · 2024-08-05Clinical Trial Update: A Study in Adults With Hereditary Angioedema (HAE) Who Currently Receive Icatibant at Home
This completed clinical trial evaluated adults with hereditary angioedema who are currently receiving icatibant at home.
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CLINICAL_TRIALS trial_result · 2024-07-30Clinical Trial Update: A Study to Review the Treatment and Outcomes of Teenagers and Adults With Non-histaminergic Angioedema With Normal C1 Inhibitor in Canada
This clinical trial update describes a completed study in Canada evaluating treatment approaches and outcomes for teenagers and adults with …
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CLINICAL_TRIALS trial_result · 2024-07-19Clinical Trial Update: A Phase III, Crossover Trial Evaluating the Efficacy and Safety of KVD900 (Sebetralstat) for On-Demand Treatment of Angioedema Attacks in Adolescent and Adult Patients With Hereditary Angioedema (HAE) [Phase 3]
Phase 3 crossover trial evaluating sebetralstat (KVD900) for on-demand treatment of hereditary angioedema attacks in adolescents and adults …
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CLINICAL_TRIALS trial_result · 2024-05-16Clinical Trial Update: Social Evaluated Cold Pressor Test in Hereditary Angioedema Patients
This clinical trial update notes the completion of a study evaluating social evaluative cold pressor testing in patients with hereditary ang…
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CLINICAL_TRIALS trial_result · 2024-05-10Clinical Trial Update: Autonomic Nervous System Profile in Hereditary Angioedema
This entry reports the completion of a clinical trial evaluating autonomic nervous system profile in patients with hereditary angioedema.
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CLINICAL_TRIALS trial_result · 2024-03-29Clinical Trial Update: Safety of Ruconest in 2-13 Year Old Hereditary Angioedema (HAE) Patients [Phase 2]
Phase 2 trial update on safety of Ruconest in children aged 2-13 with hereditary angioedema has been completed with results posted.