Hemoglobinopathy
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-03-25Clinical Trial Update: Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant Diseases [Phase 1, Phase 2]
Clinical trial update for a conditioning regimen using Campath, fludarabine, and melphalan for non-malignant diseases; currently recruiting …
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CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling [EARLY_Phase 1]
This early-phase clinical trial aims to determine red blood cell survival in sickle cell disease and other hemoglobinopathies using biotin l…
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CLINICAL_TRIALS research · 2026-01-29Clinical Trial Update: The HOPE Biobank Resource (BMT CTN 2402 HOPE)
This update announces the HOPE Biobank Resource for BMT CTN 2402, which is currently not yet recruiting and will support research in aplasti…
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CLINICAL_TRIALS research · 2026-01-28Clinical Trial Update: A Long-term Follow-up Study in Patients Who Received BEAM-101
A long-term follow-up study of patients who received BEAM-101 is ongoing, with the trial currently recruiting to assess long-term outcomes i…
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: Discarded Bone Marrow for Hematology Research
Clinical trial update notes that discarded bone marrow is being used for hematology research under St. Jude Children's Research Hospital, in…
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CLINICAL_TRIALS research · 2025-10-03Clinical Trial Update: Integrative Diagnosis for SCD and Other RADs
An ongoing clinical trial focused on integrative diagnosis for sickle cell disease and related red blood cell disorders, currently recruitin…
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CLINICAL_TRIALS research · 2025-08-07Clinical Trial Update: Long Term Follow-Up Study for Individuals With Hemoglobin Disorders After Hematopoietic Cell Transplant or Gene Therapy
Long-term follow-up study to assess outcomes in individuals with hemoglobin disorders after hematopoietic cell transplantation or gene thera…
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CLINICAL_TRIALS research · 2025-07-25Clinical Trial Update: A Phase I Study of SNH-119014 in Healthy Volunteers [Phase 1]
Phase I clinical trial update for SNH-119014 in healthy volunteers recruiting for a study on hemoglobinopathy.
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CLINICAL_TRIALS research · 2025-06-24Clinical Trial Update: TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children [Phase 2]
A Phase 2 clinical trial at Johns Hopkins All Children's Hospital is evaluating TCR alpha-beta T-cell-depleted haploidentical hematopoietic …
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CLINICAL_TRIALS research · 2025-02-18Clinical Trial Update: ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19
This clinical trials registry update reports completion of the ERN-EuroBloodNet registry documenting patients with rare red blood cell defec…
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CLINICAL_TRIALS research · 2024-08-21Clinical Trial Update: Feasibility Study to Assess an Adapted Physical Activity Program in Children, Adolescents and Young Adults Requiring Hematopoietic Stem Cell Transplantation [NA]
This ClinicalTrials.gov update reports a completed feasibility study evaluating an adapted physical activity program for children, adolescen…
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CLINICAL_TRIALS research · 2024-06-03Clinical Trial Update: Safety and Efficacy of RM-004 Cells for Hemoglobin H-Constant Spring Disease [EARLY_Phase 1]
An early Phase 1 trial evaluating the safety and potential efficacy of RM-004 cell therapy for Alpha-thalassemia with Hemoglobin H disease d…