Gm3 Synthase Deficiency
📧 Sign up to get email alerts when something new happens for Gm3 Synthase Deficiency.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2019-02-07Clinical Trial Update: Oral Supplementation of Gangliosides to Treat a Rare Metabolic Disorder [NA]
A clinical trial update indicates that oral ganglioside supplementation is being studied to treat GM3 Synthase Deficiency, a rare metabolic …