Genetic Rare Disease

Top drugs studied for this disease

All Approvals Safety alerts Label changes Trial results Research Guidance Withdrawals

CLINICAL_TRIALS trial_result · 2023-02-08
Clinical Trial Update: Targeted Busulfan, Fludarabine Conditioning Regimen for Hematopoietic Stem Cell Transplantation in GRD [Phase 1, Phase 2]
A Phase 1/2 trial evaluating a targeted busulfan and fludarabine conditioning regimen for hematopoietic stem cell transplantation in genetic…