Familial Chylomicronemia Syndrome
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CLINICAL_TRIALS research · 2026-02-11Clinical Trial Update: CS-121 APOC3 Base Editing in FCS [EARLY_Phase 1]
Early-phase trial update for CS-121 APOC3 base editing for familial chylomicronemia syndrome, currently recruiting.
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CLINICAL_TRIALS research · 2026-01-28Clinical Trial Update: CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia [EARLY_Phase 1]
CS-121 APOC3 base editing for hyperchylomicronemia in children and adolescents is in EARLY Phase 1 and currently recruiting.
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CLINICAL_TRIALS research · 2025-12-12Clinical Trial Update: A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRX) Administered to Adults With Familial Chylomicronemia Syndrome (FCS) Previously Treated With Volanesorsen [Phase 3]
Phase 3 trial update for Olezarsen in adults with Familial chylomicronemia syndrome (FCS) who were previously treated with Volanesorsen; the…
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CLINICAL_TRIALS research · 2025-12-12Clinical Trial Update: A Study of Olezarsen (Formerly Known as AKCEA-APOCIII-LRx) in Participants With Familial Chylomicronemia Syndrome (FCS) [Phase 3]
A Phase 3 trial update for olezarsen (AKCEA-APOCIII-LRx) in Familial Chylomicronemia Syndrome indicates the study is active but not currentl…