Familial Amyloidosis
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CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: Comprehensive Program for Hereditary Transthyretin Amyloidosis
Clinical trial update announcing a comprehensive program for hereditary transthyretin amyloidosis that is currently recruiting.
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CLINICAL_TRIALS trial_result · 2021-12-21Clinical Trial Update: Patisiran in Patients With Hereditary Transthyretin-mediated Amyloidosis (hATTR Amyloidosis) Disease Progression Post-Liver Transplant [Phase 3]
Phase 3 trial evaluating patisiran in hereditary transthyretin-mediated amyloidosis patients with disease progression after liver transplant…
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CLINICAL_TRIALS trial_result · 2017-03-17Clinical Trial Update: The Effect of Diflunisal on Familial Amyloidosis [Phase 2, Phase 3]
This update reports the completion and results posting of phase 2 and phase 3 trials evaluating diflunisal for familial amyloid polyneuropat…