Dysferlinopathy
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CLINICAL_TRIALS research · 2025-06-27Clinical Trial Update: Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) in the RF
A clinical trial in the Russian Federation is enrolling by invitation to study the immunological, morphological, and genetic characteristics…
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CLINICAL_TRIALS trial_result · 2025-06-24Clinical Trial Update: Observational Cohort Study of Dysferlinopathy in China
An observational cohort study of dysferlinopathy conducted in China has completed data collection and is reporting results.
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CLINICAL_TRIALS trial_result · 2015-09-02Clinical Trial Update: Deflazacort in Dysferlinopathies [Phase 2, Phase 3]
Phase 2 and Phase 3 clinical trials evaluating deflazacort for dysferlinopathies (Limb-girdle muscular dystrophy type 2B and Miyoshi myopath…