Duchenne Muscular Dystrophy
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CLINICAL_TRIALS trial_result · 2015-10-19Clinical Trial Update: Phase III Study of Idebenone in Duchenne Muscular Dystrophy (DMD) [Phase 3]
Phase III study of idebenone for Duchenne muscular dystrophy has completed and results were posted in 2015.
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CLINICAL_TRIALS research · 2015-10-15Clinical Trial Update: Correlation Between Respiratory Impairment and Phonemes Alteration in Dystrophinopathy Patients With Respiratory Failure
This completed clinical trial update documents a study evaluating the correlation between respiratory impairment and phoneme alterations in …
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CLINICAL_TRIALS trial_result · 2015-10-06Clinical Trial Update: Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients [Phase 1, Phase 2]
Phase 1/2 dose-ranging study of AVI-4658 (eteplirsen) to induce dystrophin expression in Duchenne muscular dystrophy patients; results were …
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CLINICAL_TRIALS trial_result · 2015-09-03Clinical Trial Update: Phase II Study of NPC-14 (Arbekacin Sulfate) to Explore Safety, Tolerability, and Efficacy in Duchenne Muscular Dystrophy [Phase 2]
Phase II clinical trial update for NPC-14 (Arbekacin Sulfate) assessing safety, tolerability, and efficacy in Duchenne muscular dystrophy, s…
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CLINICAL_TRIALS trial_result · 2015-08-26Clinical Trial Update: Modified Diet Trial: A Study of SMT C1100 in Paediatric Patients With DMD Who Follow a Balanced Diet [Phase 1]
Phase 1 clinical trial update for SMT C1100 in pediatric Duchenne muscular dystrophy patients on a balanced diet; the study completed.
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CLINICAL_TRIALS trial_result · 2015-08-07Clinical Trial Update: Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformin [Phase 1]
Phase 1 trial in Duchenne muscular dystrophy reports improved muscle function with a combination of L-Arginine and metformin.
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CLINICAL_TRIALS research · 2015-07-28Clinical Trial Update: Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping
An update on the Duchenne Muscular Dystrophy tissue bank for exon skipping (NCT01772043). The current trial status is unknown, and the spons…
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CLINICAL_TRIALS trial_result · 2015-07-01Clinical Trial Update: Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2 [Phase 1]
Phase 1-2 trial assessing the efficacy of stem cell therapy in ambulatory and non-ambulatory children with Duchenne Muscular Dystrophy.
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CLINICAL_TRIALS trial_result · 2015-05-28Clinical Trial Update: Evaluation of a Mechanical Device During Acute Respiratory Failure in Patients With Neuromuscular Disorders [Phase 3]
Phase 3 evaluation of a mechanical device for acute respiratory failure in patients with Duchenne muscular dystrophy and amyotrophic lateral…
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CLINICAL_TRIALS trial_result · 2015-05-27Clinical Trial Update: Eplerenone for Subclinical Cardiomyopathy in Duchenne Muscular Dystrophy [NA]
Completed results of a clinical trial evaluating eplerenone for subclinical cardiomyopathy in Duchenne muscular dystrophy, with results post…
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CLINICAL_TRIALS trial_result · 2015-05-19Clinical Trial Update: Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy
A completed clinical trial analyzed gait biomechanics in individuals with Duchenne muscular dystrophy. The study reports on gait analysis da…
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CLINICAL_TRIALS research · 2015-05-07Clinical Trial Update: Upper Limb Assessment in Duchenne Muscular Dystrophy
Clinical trial update on evaluating upper limb function in Duchenne muscular dystrophy; no results reported yet.
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CLINICAL_TRIALS trial_result · 2015-05-04Clinical Trial Update: Myocardial Fibrosis Progression in Duchenne and Becker Muscular Dystrophy - ACE Inhibitor Therapy Trial [Phase 3]
Phase 3 trial evaluating ACE inhibitor therapy for myocardial fibrosis in Duchenne muscular dystrophy and Becker muscular dystrophy has comp…
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CLINICAL_TRIALS trial_result · 2015-04-09Clinical Trial Update: Phase I/II Study of PRO044 in Duchenne Muscular Dystrophy (DMD) [Phase 1, Phase 2]
A Phase I/II study of PRO044 for Duchenne Muscular Dystrophy has completed with results posted in 2015.
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CLINICAL_TRIALS trial_result · 2015-03-13Clinical Trial Update: Duchenne Muscular Dystrophy Clinical Trial [NA]
This clinical trial update notes that a Duchenne Muscular Dystrophy study sponsored by Alan Neuromedical Technologies, LLC has completed and…
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CLINICAL_TRIALS trial_result · 2015-03-09Clinical Trial Update: Safety Study of Transvenous Limb Perfusion in Human Muscular Dystrophy [Phase 1]
Phase 1 safety study evaluating transvenous limb perfusion for muscular dystrophy has completed and results were posted in 2015.
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CLINICAL_TRIALS trial_result · 2015-02-26Clinical Trial Update: Sedation During Muscle Biopsy in Patients With Duchenne Muscular Dystrophy [NA]
This update reports results from a completed clinical trial examining sedation during muscle biopsy in patients with Duchenne Muscular Dystr…
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CLINICAL_TRIALS withdrawal · 2015-02-18Clinical Trial Update: A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophy [Phase 2]
A Phase 2 trial evaluating chronotherapy of corticosteroids in Duchenne muscular dystrophy has been withdrawn.
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CLINICAL_TRIALS withdrawal · 2015-02-04Clinical Trial Update: Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
A clinical trial investigating test-retest reliability of pulmonary function tests in patients with Duchenne muscular dystrophy has been wit…
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CLINICAL_TRIALS trial_result · 2014-11-07Clinical Trial Update: Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular Dystrophy [Phase 1, Phase 2]
This clinical trial update assesses the efficacy of umbilical cord-derived mesenchymal stem cells in Duchenne muscular dystrophy in Phase 1/…
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CLINICAL_TRIALS research · 2014-09-17Clinical Trial Update: Study Safety and Efficacy of Bone Marrow Derived Autologous Cells for the Treatment of Muscular Dystrophy. [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating autologous bone marrow-derived cells for muscular dystrophy, including Duchenne muscular dystrophy.…
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CLINICAL_TRIALS trial_result · 2014-09-17Clinical Trial Update: Study Safety and Efficacy of BMMNC for the Patient With Duchenne Muscular Dystrophy [Phase 1, Phase 2]
A clinical trial update evaluating the safety and efficacy of bone marrow mononuclear cells (BMMNC) for Duchenne muscular dystrophy in Phase…
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CLINICAL_TRIALS trial_result · 2014-08-27Clinical Trial Update: A Phase 1b Study of SMT C1100 in Subjects With Duchenne Muscular Dystrophy (DMD) [Phase 1]
A Phase 1b study of SMT C1100 in Duchenne Muscular Dystrophy has completed.
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CLINICAL_TRIALS trial_result · 2014-08-25Clinical Trial Update: Phase II Doubleblind Exploratory Study of GSK2402968 in Ambulant Subjects With Duchenne Muscular Dystrophy [Phase 2]
A Phase II double-blind exploratory study of GSK2402968 in ambulant Duchenne muscular dystrophy subjects has completed; results are not deta…
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EMA approval · 2014-05-23European Medicines Agency recommends first-in-class medicine for treatment of Duchenne muscular dystrophy
EMA recommends a first-in-class medicine for Duchenne muscular dystrophy, signaling potential approval for a novel mechanism in this indicat…